Therapeutic Approaches
May 21, 2020
How does Omav Affect Your Cells
Joseph Johnson, Children’s Hospital of Philadelphia
CRISPR/Cas9 Gene Editing of Friedreich’s Ataxia Patients’ Blood Stem
Cells
Joseph Rainaldi, University of California- San Diego
Safe Delivery of Frataxin Gene to Mouse Brain and Body Using Engineered
AAVs
Acacia Hori , Cal Tech
https://www.curefa.org/pdf/research/FA-Research-Flash-Talk-Series.pdf
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